NCATS Researchers’ New Approach to Measure Gene Activity Could Speed Search for Rare Disease Therapies

NCATS scientists design an innovative test to find potential treatments for Charcot-Marie-Tooth disease (CMT), one of the most common inherited neurological diseases, opening new pathways for rare diseases research.

2021-03-23 NCATS /news-events/news/ncats-researchers-new-approach-to-measure-gene-activity-could-speed-search-for-rare-disease-therapies